Advancing Science, Enhancing Lives
We are leading the development of next-generation RNA therapeutics to be more efficient, safer, and accessible for treating inherited rare and acquired diseases.
Home of RNA Therapeutics
We provide highly effective treatments for a diverse array of acquired and genetic illnesses.

Precision RNA Therapeutics
As a leading innovator in the field of precision RNA therapy, we harness cutting-edge antisense technology to redefine possibilities in modern medicine.

Led by World-renowned Experts
Guided by globally acclaimed experts with unparalleled expertise in RNA therapeutics, including advanced antisense oligonucleotide chemistries and precision manufacturing.
“Our approach to precision RNA therapy represents a paradigm shift in the way we think about treating diseases.”
– Prof. Marvin H. Caruthers & Assoc. Prof. Rakesh N. Veedu, Co-Founders


RNA Therapeutics
We develop antisense oligonucleotides (ASOs), small RNA-based drugs that bind to messenger RNA (mRNA) to regulate the production of disease-causing proteins.
Disease Areas
Through rigorous research and innovation, we’ve uncovered groundbreaking targets that hold the power to transform how we treat a diverse range of diseases.

Committed to Health & Wellbeing
Driven by innovation, we are redefining the future of disease treatment and transforming lives through groundbreaking advancements.

Finding Cure through Therapeutic Innovation
Our team is dedicated to developing breakthrough, disease-modifying therapeutics that are safer, more effective, and accessible.

Let’s have a chat
Have questions or want to connect? Reach out to our team for more information on our innovative solutions and opportunities.