
Our Disease Areas
We target inherited rare and acquired diseases with innovative RNA therapeutics, offering hope to patients with chronic and debilitating conditions.

Type 2 Diabetes
Type 2 diabetes (T2D) is a chronic, metabolic disease in which blood sugar levels become elevated due to the body’s cells becoming resistant to insulin.

Rett Syndrome
Rett syndrome (RTT) is a rare progressive neurodevelopmental disorder affecting approximately 1 in 10,000 female births worldwide.
Our Pipeline

“This would be a new RNA therapy for type 2 diabetes, with the potential to improve glucose control and reduce the burden of disease.”
-Dr. Bu Yeap, Clinical Advisor
